{"id":"doi:10.1016/j.mayocpiqo.2026.100755","kind":"article","title":"From Vision to Validation: The Journey of Tofersen in Superoxide Dismutase 1 Gene-Associated Amyotrophic Lateral Sclerosis","authors":["Oskarsson B","Heckman MG"],"author_count":2,"year":2026,"published":"2026-09-07","venue":"Mayo Clinic proceedings. Innovations, quality & outcomes","cited_by":0,"doi":"10.1016/j.mayocpiqo.2026.100755","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1016/j.mayocpiqo.2026.100755","archive_url":"https://space-kitty.com/papers/doi:10.1016/j.mayocpiqo.2026.100755","updated":null,"pmid":"42751043","pmcid":null,"openalex_id":null,"pdf_url":null,"abstract":null,"abstract_license":null,"license":"CC-BY","is_open_access":false,"retracted":false,"peer_reviewed":null,"categories":[],"details":null,"provenance":"europepmc","attribution":"Metadata: Europe PMC (EMBL-EBI).","topics":[{"slug":"neurodegeneration","name":"Alzheimer's, Parkinson's & Neurodegeneration","domain_slug":"medicine"}],"cited_in_dossiers":[]}