{"id":"doi:10.1016/j.preteyeres.2010.04.002","kind":"review","title":"Leber congenital amaurosis due to RPE65 mutations and its treatment with gene therapy","authors":["Artur V. Cideciyan"],"author_count":1,"year":2010,"published":"2010-04-26","venue":"Progress in Retinal and Eye Research","cited_by":256,"doi":"10.1016/j.preteyeres.2010.04.002","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1016/j.preteyeres.2010.04.002","archive_url":"https://space-kitty.com/papers/doi:10.1016/j.preteyeres.2010.04.002","updated":null,"pmid":"20399883","pmcid":null,"openalex_id":"W1970654757","pdf_url":null,"abstract":null,"abstract_license":null,"license":null,"is_open_access":true,"retracted":false,"peer_reviewed":null,"categories":["Retinal Development and Disorders"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-cell-therapy","name":"Gene & Cell Therapy","domain_slug":"medicine"}],"cited_in_dossiers":[]}