{"id":"doi:10.1016/j.ymthe.2016.12.006","kind":"article","title":"CRISPR/Cas9-Mediated Genome Editing as a Therapeutic Approach for Leber Congenital Amaurosis 10","authors":["Guo-Xiang Ruan","Elizabeth Barry","Dan Yu","Michael Lukason","Seng H. Cheng","Abraham Scaria"],"author_count":6,"year":2017,"published":"2017-01-18","venue":"Molecular Therapy","cited_by":270,"doi":"10.1016/j.ymthe.2016.12.006","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1016/j.ymthe.2016.12.006","archive_url":"https://space-kitty.com/papers/doi:10.1016/j.ymthe.2016.12.006","updated":null,"pmid":"28109959","pmcid":null,"openalex_id":"W2575178850","pdf_url":"http://www.cell.com/article/S1525001616454286/pdf","abstract":null,"abstract_license":null,"license":"cc-by-nc-nd","is_open_access":true,"retracted":false,"peer_reviewed":null,"categories":["CRISPR and Genetic Engineering"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-editing-therapies","name":"CRISPR & Gene-Editing Therapies","domain_slug":"medicine"}],"cited_in_dossiers":[]}