{"id":"doi:10.1016/j.ymthe.2020.01.005","kind":"article","title":"Treatment of a Mouse Model of ALS by In Vivo Base Editing","authors":["Colin K.W. Lim","Michael Gapinske","Alexandra K. Brooks","Wendy S. Woods","Jackson E. Powell","M. Alejandra Zeballos C.","Jackson Winter","Pablo Pérez‐Piñera","Thomas Gaj"],"author_count":9,"year":2020,"published":"2020-01-13","venue":"Molecular Therapy","cited_by":225,"doi":"10.1016/j.ymthe.2020.01.005","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1016/j.ymthe.2020.01.005","archive_url":"https://space-kitty.com/papers/doi:10.1016/j.ymthe.2020.01.005","updated":null,"pmid":"31991108","pmcid":null,"openalex_id":"W3000070051","pdf_url":null,"abstract":null,"abstract_license":null,"license":"cc-by-nc-nd","is_open_access":true,"retracted":false,"peer_reviewed":null,"categories":["CRISPR and Genetic Engineering"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-cell-therapy","name":"Gene & Cell Therapy","domain_slug":"medicine"}],"cited_in_dossiers":[]}