{"id":"doi:10.1038/mt.2010.274","kind":"article","title":"Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins","authors":["Amit Chunilal Nathwani","Cecilia Rosales","Jenny McIntosh","Ghasem Rastegar Lari","Devhrut Nathwani","Deepak Raj","Sushmita Nawathe","Simon N. Waddington","Roderick Terry Bronson","Scott Jackson","Robert E. Donahue","Katherine A. High","Federico Mingozzi","Catherine Y. Ng","Junfang Zhou","Yunyu Spence","M. Beth McCarville","Marc B. Valentine","James A. Allay","John Coleman","Susan Sleep","John T. Gray","Arthur W. Nienhuis","Andrew M. Davidoff"],"author_count":24,"year":2011,"published":"2011-01-18","venue":"Molecular Therapy","cited_by":345,"doi":"10.1038/mt.2010.274","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1038/mt.2010.274","archive_url":"https://space-kitty.com/papers/doi:10.1038/mt.2010.274","updated":null,"pmid":"21245849","pmcid":null,"openalex_id":"W2088410491","pdf_url":"http://www.cell.com/article/S152500161631886X/pdf","abstract":null,"abstract_license":null,"license":"cc-by-nc-nd","is_open_access":true,"retracted":false,"peer_reviewed":null,"categories":["Virus-based gene therapy research"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-cell-therapy","name":"Gene & Cell Therapy","domain_slug":"medicine"}],"cited_in_dossiers":[]}