{"id":"doi:10.1038/mt.2011.237","kind":"article","title":"Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector","authors":["Dawn E. Bowles","Scott McPhee","Chengwen Li","Steven James Gray","Jade Samulski","Angelique S. Camp","Juan Li","Bing Wang","Paul Edward Monahan","Joseph E. Rabinowitz","Joshua C. Grieger","Lakshmanan Govindasamy A","Mavis Agbandje‐McKenna","Xiao Xiao","Richard Jude Samulski"],"author_count":15,"year":2011,"published":"2011-11-08","venue":"Molecular Therapy","cited_by":400,"doi":"10.1038/mt.2011.237","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1038/mt.2011.237","archive_url":"https://space-kitty.com/papers/doi:10.1038/mt.2011.237","updated":null,"pmid":"22068425","pmcid":null,"openalex_id":"W2015870495","pdf_url":"http://www.cell.com/article/S152500161630497X/pdf","abstract":null,"abstract_license":null,"license":"cc-by-nc-nd","is_open_access":true,"peer_reviewed":null,"categories":["Virus-based gene therapy research"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-cell-therapy","name":"Gene & Cell Therapy","domain_slug":"medicine"}],"cited_in_dossiers":[]}