{"id":"doi:10.1038/mt.2014.200","kind":"article","title":"A Phase 1/2a Follistatin Gene Therapy Trial for Becker Muscular Dystrophy","authors":["Jerry R. Mendell","Zarife Sahenk","Vinod Malik","Ana M Gomez","Kevin M. Flanigan","Linda Pax Lowes","Lindsay N. Alfano","Katherine Berry","Eric Meadows","Sarah Lewis","Lyndsey Braun","Kim Shontz","Maria Rouhana","Kelly Reed Clark","Xiomara Q. Rosales","Samiah A. Al-Zaidy","Alessandra Govoni","Louise R. Rodino‐Klapac","Mark J Hogan","Brian K. Kaspar"],"author_count":20,"year":2014,"published":"2014-10-17","venue":"Molecular Therapy","cited_by":246,"doi":"10.1038/mt.2014.200","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1038/mt.2014.200","archive_url":"https://space-kitty.com/papers/doi:10.1038/mt.2014.200","updated":null,"pmid":"25322757","pmcid":null,"openalex_id":"W2039035739","pdf_url":null,"abstract":null,"abstract_license":null,"license":"cc-by-nc-nd","is_open_access":true,"retracted":false,"peer_reviewed":null,"categories":["Muscle Physiology and Disorders"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-cell-therapy","name":"Gene & Cell Therapy","domain_slug":"medicine"}],"cited_in_dossiers":[]}