{"id":"doi:10.1038/mt.2015.192","kind":"article","title":"CRISPR-mediated Genome Editing Restores Dystrophin Expression and Function in mdx Mice","authors":["Li ming Xu","Ki Ho Park","Lixia Zhao","Jing Xu","Mona El Refaey","Yandi Gao","Hua Zhu C","Jianjie Ma","Renzhi Han"],"author_count":9,"year":2015,"published":"2015-10-09","venue":"Molecular Therapy","cited_by":244,"doi":"10.1038/mt.2015.192","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1038/mt.2015.192","archive_url":"https://space-kitty.com/papers/doi:10.1038/mt.2015.192","updated":null,"pmid":"26449883","pmcid":null,"openalex_id":"W2205893844","pdf_url":null,"abstract":null,"abstract_license":null,"license":"cc-by-nc-nd","is_open_access":true,"retracted":false,"peer_reviewed":null,"categories":["CRISPR and Genetic Engineering"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-editing-therapies","name":"CRISPR & Gene-Editing Therapies","domain_slug":"medicine"}],"cited_in_dossiers":[]}