{"id":"doi:10.1038/nature20134","kind":"article","title":"CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cells","authors":["Daniel P. Dever","Rasmus Otkjær Bak","Andreas Reinisch","Joab Camarena","Gabriel C. Washington","Carmencita E. Nicolas","Mara Pavel-Dinu","Nivi Saxena","Alec B. Wilkens","Sruthi Mantri","Nobuko Uchida","Ayal Hendel","Anupama Narla","Ravindra Majeti","Kenneth I. Weinberg","Matthew Hebden Porteus"],"author_count":16,"year":2016,"published":"2016-11-04","venue":"Nature","cited_by":864,"doi":"10.1038/nature20134","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1038/nature20134","archive_url":"https://space-kitty.com/papers/doi:10.1038/nature20134","updated":null,"pmid":"27820943","pmcid":null,"openalex_id":"W2547418311","pdf_url":null,"abstract":null,"abstract_license":null,"license":null,"is_open_access":true,"retracted":false,"peer_reviewed":null,"categories":["CRISPR and Genetic Engineering"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-editing-therapies","name":"CRISPR & Gene-Editing Therapies","domain_slug":"medicine"}],"cited_in_dossiers":[]}