{"id":"doi:10.1038/nm.4170","kind":"article","title":"A genome-editing strategy to treat β-hemoglobinopathies that recapitulates a mutation associated with a benign genetic condition","authors":["Elizabeth A. Traxler","Yu Yao","Yong‐Dong Wang","Kaitly J. Woodard","Ryo Kurita","Yukio Nakamura","Jim R. Hughes","Ross C. Hardison","Gerd A. Blobel","Chunliang Li","Mitchell J. Weiss"],"author_count":11,"year":2016,"published":"2016-08-15","venue":"Nature Medicine","cited_by":366,"doi":"10.1038/nm.4170","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1038/nm.4170","archive_url":"https://space-kitty.com/papers/doi:10.1038/nm.4170","updated":null,"pmid":"27525524","pmcid":null,"openalex_id":"W2511090954","pdf_url":null,"abstract":null,"abstract_license":null,"license":null,"is_open_access":true,"peer_reviewed":null,"categories":["Hemoglobinopathies and Related Disorders"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-editing-therapies","name":"CRISPR & Gene-Editing Therapies","domain_slug":"medicine"}],"cited_in_dossiers":[]}