{"id":"doi:10.1056/nejmoa2307798","kind":"article","title":"Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne’s Muscular Dystrophy","authors":["Angela Lek","Brenda L. Y. Wong","Allison M. Keeler","Meghan Blackwood","Kaiyue Ma","Shushu Huang","Katelyn Sylvia","Ana Rita Batista","Rebecca Artinian","Danielle Kokoski","Shestruma Parajuli","Juan Putra","Chrystalle Katte Carreon","Hart G.W. Lidov","Keryn G. Woodman","Sander Pajusalu","Janelle M. Spinazzola","T. F. Gallagher","Joan M. LaRovere","Diane E Balderson","Lauren Black","Keith A. Sutton","Richard Horgan","Monkol Lek","Terence R. Flotte"],"author_count":25,"year":2023,"published":"2023-09-27","venue":"New England Journal of Medicine","cited_by":318,"doi":"10.1056/nejmoa2307798","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1056/nejmoa2307798","archive_url":"https://space-kitty.com/papers/doi:10.1056/nejmoa2307798","updated":null,"pmid":"37754285","pmcid":null,"openalex_id":"W4387077861","pdf_url":"https://pmc.ncbi.nlm.nih.gov/articles/PMC11288170/pdf/nihms-1998854.pdf","abstract":null,"abstract_license":null,"license":null,"is_open_access":true,"retracted":false,"peer_reviewed":null,"categories":["Virus-based gene therapy research"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-cell-therapy","name":"Gene & Cell Therapy","domain_slug":"medicine"}],"cited_in_dossiers":[]}