{"id":"doi:10.1056/nejmoa2309676","kind":"article","title":"Exagamglogene Autotemcel for Severe Sickle Cell Disease","authors":["Haydar Frangoul","Franco Locatelli","Akshay Sharma","Monica Bhatia","Markus Y. Mapara","Lyndsay Molinari","Donna Ann Wall","Robert I. Liem","Paul T. Telfer","Ami J. Shah","Marina Cavazzana","Selim Corbacioglu","Damiano Rondelli","Roland Meisel","Laurence Dedeken","Stephan Lobitz","Mariane de Montalembert","Martin H. Steinberg","Mark C. Walters","Michael J. Eckrich","Suzan Imren","Laura Bower","Christopher Simard","Weiyu Zhou","Fengjuan Xuan"],"author_count":28,"year":2024,"published":"2024-04-24","venue":"New England Journal of Medicine","cited_by":492,"doi":"10.1056/nejmoa2309676","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1056/nejmoa2309676","archive_url":"https://space-kitty.com/papers/doi:10.1056/nejmoa2309676","updated":null,"pmid":"38661449","pmcid":null,"openalex_id":"W4395068280","pdf_url":null,"abstract":null,"abstract_license":null,"license":null,"is_open_access":false,"retracted":false,"peer_reviewed":null,"categories":["Hemoglobinopathies and Related Disorders"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-editing-therapies","name":"CRISPR & Gene-Editing Therapies","domain_slug":"medicine"}],"cited_in_dossiers":[{"slug":"gene-editing-therapies","title":"CRISPR & Gene-Editing Therapies: State of the Field (October 2026)","url":"https://space-kitty.com/dossiers/gene-editing-therapies"}]}