{"id":"doi:10.1126/science.aad5143","kind":"article","title":"In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy","authors":["Christopher E. Nelson","Chady H. Hakim","David G. Ousterout","Pratiksha I. Thakore","Eirik A. Moreb","Ruth M. Castellanos Rivera","Sarina Madhavan","Xiufang Pan","F. Ann Ran","Winston X. Yan","Aravind Asokan","Feng Zhang","Dongsheng Duan","Charles A. Gersbach"],"author_count":14,"year":2015,"published":"2015-12-31","venue":"Science","cited_by":1143,"doi":"10.1126/science.aad5143","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1126/science.aad5143","archive_url":"https://space-kitty.com/papers/doi:10.1126/science.aad5143","updated":null,"pmid":"26721684","pmcid":null,"openalex_id":"W2208696160","pdf_url":null,"abstract":null,"abstract_license":null,"license":null,"is_open_access":true,"retracted":false,"peer_reviewed":null,"categories":["CRISPR and Genetic Engineering"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-editing-therapies","name":"CRISPR & Gene-Editing Therapies","domain_slug":"medicine"}],"cited_in_dossiers":[]}