{"id":"doi:10.1172/jci41615","kind":"article","title":"CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy","authors":["Marco A. Passini","Jie Bu","Eric M. Roskelley","Amy M. Richards","S. Pablo Sardi","Catherine R. O’Riordan","Katherine Wood Klinger","Lamya S. Shihabuddin","Seng H. Cheng"],"author_count":9,"year":2010,"published":"2010-03-16","venue":"Journal of Clinical Investigation","cited_by":292,"doi":"10.1172/jci41615","arxiv_id":null,"nct_id":null,"source_url":"https://doi.org/10.1172/jci41615","archive_url":"https://space-kitty.com/papers/doi:10.1172/jci41615","updated":null,"pmid":"20234094","pmcid":null,"openalex_id":"W2088820444","pdf_url":null,"abstract":null,"abstract_license":null,"license":null,"is_open_access":true,"retracted":false,"peer_reviewed":null,"categories":["Neurogenetic and Muscular Disorders Research"],"details":null,"provenance":"openalex","attribution":"Metadata and citation counts: OpenAlex (CC0).","topics":[{"slug":"gene-cell-therapy","name":"Gene & Cell Therapy","domain_slug":"medicine"}],"cited_in_dossiers":[]}