{"id":"nct:NCT07408583","kind":"trial","title":"Prenatal Transplantation for Fetuses With Fanconi Anemia","authors":["Agnieszka Czechowicz"],"author_count":1,"year":2026,"published":"2026-02-13","venue":"ClinicalTrials.gov","cited_by":null,"doi":null,"arxiv_id":null,"nct_id":"NCT07408583","source_url":"https://clinicaltrials.gov/study/NCT07408583","archive_url":"https://space-kitty.com/papers/nct:NCT07408583","updated":"2026-06-16","pmid":null,"pmcid":null,"openalex_id":null,"pdf_url":null,"abstract":"The investigators aim to evaluate the safety and efficacy of in utero hematopoietic stem cell transplantation (IUHSCT) for the treatment of fetuses diagnosed with Fanconi anemia (FA) during pregnancy.","abstract_license":"ClinicalTrials.gov (U.S. National Library of Medicine), data processed 2026-10-29T09:00:05; modifications: selected fields only; whitespace normalized; brief summary truncated to 2,000 characters","license":"ClinicalTrials.gov terms (attribution, processing date, modifications noted)","is_open_access":true,"peer_reviewed":null,"categories":["Fanconi Anemia","Anemia, Hypoplastic, Congenital","Congenital Bone Marrow Failure Syndromes","Bone Marrow Failure Disorders","Genetic Diseases, Inborn","Congenital, Hereditary, and Neonatal Diseases and Abnormalities"],"details":{"acronym":null,"status":"NOT_YET_RECRUITING","phase":"PHASE1, PHASE2","study_type":"INTERVENTIONAL","enrollment":12,"sponsor":"Agnieszka Czechowicz","conditions":["Fanconi Anemia","Anemia, Hypoplastic, Congenital","Congenital Bone Marrow Failure Syndromes","Bone Marrow Failure Disorders","Genetic Diseases, Inborn","Congenital, Hereditary, and Neonatal Diseases and Abnormalities","DNA Repair-Deficiency Disorders","Cancer Predisposition Syndrome"],"interventions":["BIOLOGICAL: IUHSCT for FA-affected fetuses"],"start_date":"2028-01-01","start_date_type":"ESTIMATED","primary_completion_date":"2031-07-01","has_results":false,"data_source":"ClinicalTrials.gov","data_processed":"2026-10-29T09:00:05","modifications":"selected fields only; whitespace normalized; brief summary truncated to 2,000 characters"},"provenance":"clinicaltrials","attribution":"Source: ClinicalTrials.gov (U.S. National Library of Medicine), data processed 2026-10-29T09:00:05; modifications: selected fields only; whitespace normalized; brief summary truncated to 2,000 characters. Not a U.S. Government endorsement.","topics":[{"slug":"gene-cell-therapy","name":"Gene & Cell Therapy","domain_slug":"medicine"}],"cited_in_dossiers":[]}