{"id":"nct:NCT07489196","kind":"trial","title":"A Phase 2 Safety and Efficacy Study Evaluating CS-101 in Participants With β-Thalassemia Major","authors":["CorrectSequence Therapeutics Co., Ltd"],"author_count":1,"year":2026,"published":"2026-03-24","venue":"ClinicalTrials.gov","cited_by":null,"doi":null,"arxiv_id":null,"nct_id":"NCT07489196","source_url":"https://clinicaltrials.gov/study/NCT07489196","archive_url":"https://space-kitty.com/papers/nct:NCT07489196","updated":"2026-03-24","pmid":null,"pmcid":null,"openalex_id":null,"pdf_url":null,"abstract":"The goal of this open label, single-arm clinical study is to learn about the safety and efficacy of CS-101 in treating patients with β-Thalassemia Major","abstract_license":"ClinicalTrials.gov (U.S. National Library of Medicine), data processed 2026-10-29T09:00:05; modifications: selected fields only; whitespace normalized; brief summary truncated to 2,000 characters","license":"ClinicalTrials.gov terms (attribution, processing date, modifications noted)","is_open_access":true,"retracted":false,"peer_reviewed":null,"categories":["β-thalassemia Major"],"details":{"acronym":null,"status":"NOT_YET_RECRUITING","phase":"PHASE2","study_type":"INTERVENTIONAL","enrollment":20,"sponsor":"CorrectSequence Therapeutics Co., Ltd","conditions":["β-thalassemia Major"],"interventions":["GENETIC: CS-101 injection"],"start_date":"2026-04-05","start_date_type":"ESTIMATED","primary_completion_date":"2028-01-31","has_results":false,"data_source":"ClinicalTrials.gov","data_processed":"2026-10-29T09:00:05","modifications":"selected fields only; whitespace normalized; brief summary truncated to 2,000 characters"},"provenance":"clinicaltrials","attribution":"Source: ClinicalTrials.gov (U.S. National Library of Medicine), data processed 2026-10-29T09:00:05; modifications: selected fields only; whitespace normalized; brief summary truncated to 2,000 characters. Not a U.S. Government endorsement.","topics":[{"slug":"gene-editing-therapies","name":"CRISPR & Gene-Editing Therapies","domain_slug":"medicine"}],"cited_in_dossiers":[]}