# Treatment of retinitis pigmentosa due to MERTK mutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial

Article · Nicola G. Ghazi, Emad B. Abboud, Sawsan R. Nowilaty, Hisham Alkuraya, Abdulrahman Alhommadi, Huimin Cai, Rui Hou, Wen‐Tao Deng, Sanford L. Boye, Abdulrahman M. Almaghamsi, Fahad Al Saikhan, Hassan A. Al-Dhibi, David G. Birch, Christopher Chung, Dilek Çolak, Matthew M. LaVail, Douglas Vollrath, Kirsten E. Erger, Wen‐qiu Wang, Thomas J. Conlon, Kang Zhang, William W. Hauswirth, Fowzan Sami Alkuraya

- Archive id: doi:10.1007/s00439-016-1637-y
- Published: 2016-01-29
- Venue: Human Genetics
- DOI: https://doi.org/10.1007/s00439-016-1637-y
- PMID: 26825853
- Citations: 243
- Source URL: https://doi.org/10.1007/s00439-016-1637-y
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [Gene & Cell Therapy](https://space-kitty.com/topics/gene-cell-therapy)

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