# Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia

Article · Ding An, Jessica L. Schneller, Andrea Frassetto, Shi Liang, Xuling Zhu, Ji-Sun Park, Matt Theisen, Sue‐Jean Hong, Jenny Zhou, Raj Rajendran, Becca Levy, Rebecca Dean Howell, Gilles Besin, Vladimir Presnyak, Staci Sabnis, Kerry E. Murphy-Benenato, E. Sathyajith Kumarasinghe, Timothy Salerno, Cosmin Mihai, Christine Lukacs, Randy J. Chandler, Lin T. Guey, Charles P. Venditti, Paolo G.V. Martini

- Archive id: doi:10.1016/j.celrep.2017.11.081
- Published: 2017-12-01
- Venue: Cell Reports
- DOI: https://doi.org/10.1016/j.celrep.2017.11.081
- PMID: 29262333
- Citations: 263
- Source URL: https://doi.org/10.1016/j.celrep.2017.11.081
- PDF: http://www.cell.com/article/S2211124717317485/pdf
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [Gene & Cell Therapy](https://space-kitty.com/topics/gene-cell-therapy)

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