# From Vision to Validation: The Journey of Tofersen in Superoxide Dismutase 1 Gene-Associated Amyotrophic Lateral Sclerosis

Article · Oskarsson B, Heckman MG

- Archive id: doi:10.1016/j.mayocpiqo.2026.100755
- Published: 2026-09-07
- Venue: Mayo Clinic proceedings. Innovations, quality & outcomes
- DOI: https://doi.org/10.1016/j.mayocpiqo.2026.100755
- PMID: 42751043
- Citations: 0
- Source URL: https://doi.org/10.1016/j.mayocpiqo.2026.100755
- Provenance: europepmc

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [Alzheimer's, Parkinson's & Neurodegeneration](https://space-kitty.com/topics/neurodegeneration)

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