# Leber congenital amaurosis due to RPE65 mutations and its treatment with gene therapy

Review · Artur V. Cideciyan

- Archive id: doi:10.1016/j.preteyeres.2010.04.002
- Published: 2010-04-26
- Venue: Progress in Retinal and Eye Research
- DOI: https://doi.org/10.1016/j.preteyeres.2010.04.002
- PMID: 20399883
- Citations: 256
- Source URL: https://doi.org/10.1016/j.preteyeres.2010.04.002
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [Gene & Cell Therapy](https://space-kitty.com/topics/gene-cell-therapy)

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