# CRISPR/Cas9-Mediated Genome Editing as a Therapeutic Approach for Leber Congenital Amaurosis 10

Article · Guo-Xiang Ruan, Elizabeth Barry, Dan Yu, Michael Lukason, Seng H. Cheng, Abraham Scaria

- Archive id: doi:10.1016/j.ymthe.2016.12.006
- Published: 2017-01-18
- Venue: Molecular Therapy
- DOI: https://doi.org/10.1016/j.ymthe.2016.12.006
- PMID: 28109959
- Citations: 270
- Source URL: https://doi.org/10.1016/j.ymthe.2016.12.006
- PDF: http://www.cell.com/article/S1525001616454286/pdf
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [CRISPR & Gene-Editing Therapies](https://space-kitty.com/topics/gene-editing-therapies)

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