# Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial

Article · Robert Edward MacLaren, Markus Groppe, Alun R. Barnard, Charles L. Cottriall, Tanya Tolmachova, Leonard William Seymour, Kelly Reed Clark, Matthew J. During, Frans P.M. Cremers, Graeme Charles M. Black, Andrew John Lotery, Susan M. Downes, Andrew R. Webster, Miguel C. Seabra

- Archive id: doi:10.1016/s0140-6736(13)62117-0
- Published: 2014-01-15
- Venue: The Lancet
- DOI: https://doi.org/10.1016/s0140-6736(13)62117-0
- PMID: 24439297
- Citations: 796
- Source URL: https://doi.org/10.1016/s0140-6736(13)62117-0
- PDF: http://www.thelancet.com/article/S0140673613621170/pdf
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [Gene & Cell Therapy](https://space-kitty.com/topics/gene-cell-therapy)

Cited in dossiers:
- [Gene & Cell Therapy: State of the Field (October 2026)](https://space-kitty.com/dossiers/gene-cell-therapy)

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