# Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins

Article · Amit Chunilal Nathwani, Cecilia Rosales, Jenny McIntosh, Ghasem Rastegar Lari, Devhrut Nathwani, Deepak Raj, Sushmita Nawathe, Simon N. Waddington, Roderick Terry Bronson, Scott Jackson, Robert E. Donahue, Katherine A. High, Federico Mingozzi, Catherine Y. Ng, Junfang Zhou, Yunyu Spence, M. Beth McCarville, Marc B. Valentine, James A. Allay, John Coleman, Susan Sleep, John T. Gray, Arthur W. Nienhuis, Andrew M. Davidoff

- Archive id: doi:10.1038/mt.2010.274
- Published: 2011-01-18
- Venue: Molecular Therapy
- DOI: https://doi.org/10.1038/mt.2010.274
- PMID: 21245849
- Citations: 345
- Source URL: https://doi.org/10.1038/mt.2010.274
- PDF: http://www.cell.com/article/S152500161631886X/pdf
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [Gene & Cell Therapy](https://space-kitty.com/topics/gene-cell-therapy)

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