# Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

Article · Dawn E. Bowles, Scott McPhee, Chengwen Li, Steven James Gray, Jade Samulski, Angelique S. Camp, Juan Li, Bing Wang, Paul Edward Monahan, Joseph E. Rabinowitz, Joshua C. Grieger, Lakshmanan Govindasamy A, Mavis Agbandje‐McKenna, Xiao Xiao, Richard Jude Samulski

- Archive id: doi:10.1038/mt.2011.237
- Published: 2011-11-08
- Venue: Molecular Therapy
- DOI: https://doi.org/10.1038/mt.2011.237
- PMID: 22068425
- Citations: 400
- Source URL: https://doi.org/10.1038/mt.2011.237
- PDF: http://www.cell.com/article/S152500161630497X/pdf
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [Gene & Cell Therapy](https://space-kitty.com/topics/gene-cell-therapy)

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