# A Phase 1/2a Follistatin Gene Therapy Trial for Becker Muscular Dystrophy

Article · Jerry R. Mendell, Zarife Sahenk, Vinod Malik, Ana M Gomez, Kevin M. Flanigan, Linda Pax Lowes, Lindsay N. Alfano, Katherine Berry, Eric Meadows, Sarah Lewis, Lyndsey Braun, Kim Shontz, Maria Rouhana, Kelly Reed Clark, Xiomara Q. Rosales, Samiah A. Al-Zaidy, Alessandra Govoni, Louise R. Rodino‐Klapac, Mark J Hogan, Brian K. Kaspar

- Archive id: doi:10.1038/mt.2014.200
- Published: 2014-10-17
- Venue: Molecular Therapy
- DOI: https://doi.org/10.1038/mt.2014.200
- PMID: 25322757
- Citations: 246
- Source URL: https://doi.org/10.1038/mt.2014.200
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [Gene & Cell Therapy](https://space-kitty.com/topics/gene-cell-therapy)

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