# CRISPR-mediated Genome Editing Restores Dystrophin Expression and Function in mdx Mice

Article · Li ming Xu, Ki Ho Park, Lixia Zhao, Jing Xu, Mona El Refaey, Yandi Gao, Hua Zhu C, Jianjie Ma, Renzhi Han

- Archive id: doi:10.1038/mt.2015.192
- Published: 2015-10-09
- Venue: Molecular Therapy
- DOI: https://doi.org/10.1038/mt.2015.192
- PMID: 26449883
- Citations: 244
- Source URL: https://doi.org/10.1038/mt.2015.192
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [CRISPR & Gene-Editing Therapies](https://space-kitty.com/topics/gene-editing-therapies)

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