# CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cells

Article · Daniel P. Dever, Rasmus Otkjær Bak, Andreas Reinisch, Joab Camarena, Gabriel C. Washington, Carmencita E. Nicolas, Mara Pavel-Dinu, Nivi Saxena, Alec B. Wilkens, Sruthi Mantri, Nobuko Uchida, Ayal Hendel, Anupama Narla, Ravindra Majeti, Kenneth I. Weinberg, Matthew Hebden Porteus

- Archive id: doi:10.1038/nature20134
- Published: 2016-11-04
- Venue: Nature
- DOI: https://doi.org/10.1038/nature20134
- PMID: 27820943
- Citations: 864
- Source URL: https://doi.org/10.1038/nature20134
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [CRISPR & Gene-Editing Therapies](https://space-kitty.com/topics/gene-editing-therapies)

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