# A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice

Article · Yang Yang, Lili Wang, Peter L. Bell, Deirdre McMenamin, Zhenning He, John White, Hongwei Yu, Chenyu Xu, Hiroki Morizono, Kiran Musunuru, Mark L. Batshaw, James M. Wilson

- Archive id: doi:10.1038/nbt.3469
- Published: 2016-02-01
- Venue: Nature Biotechnology
- DOI: https://doi.org/10.1038/nbt.3469
- PMID: 26829317
- Citations: 556
- Source URL: https://doi.org/10.1038/nbt.3469
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [Gene & Cell Therapy](https://space-kitty.com/topics/gene-cell-therapy)

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