# A genome-editing strategy to treat β-hemoglobinopathies that recapitulates a mutation associated with a benign genetic condition

Article · Elizabeth A. Traxler, Yu Yao, Yong‐Dong Wang, Kaitly J. Woodard, Ryo Kurita, Yukio Nakamura, Jim R. Hughes, Ross C. Hardison, Gerd A. Blobel, Chunliang Li, Mitchell J. Weiss

- Archive id: doi:10.1038/nm.4170
- Published: 2016-08-15
- Venue: Nature Medicine
- DOI: https://doi.org/10.1038/nm.4170
- PMID: 27525524
- Citations: 366
- Source URL: https://doi.org/10.1038/nm.4170
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [CRISPR & Gene-Editing Therapies](https://space-kitty.com/topics/gene-editing-therapies)

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