# Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges

Review · Federico Mingozzi, Katherine A. High

- Archive id: doi:10.1038/nrg2988
- Published: 2011-04-18
- Venue: Nature Reviews Genetics
- DOI: https://doi.org/10.1038/nrg2988
- PMID: 21499295
- Citations: 893
- Source URL: https://doi.org/10.1038/nrg2988
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [Gene & Cell Therapy](https://space-kitty.com/topics/gene-cell-therapy)

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