# Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne’s Muscular Dystrophy

Article · Angela Lek, Brenda L. Y. Wong, Allison M. Keeler, Meghan Blackwood, Kaiyue Ma, Shushu Huang, Katelyn Sylvia, Ana Rita Batista, Rebecca Artinian, Danielle Kokoski, Shestruma Parajuli, Juan Putra, Chrystalle Katte Carreon, Hart G.W. Lidov, Keryn G. Woodman, Sander Pajusalu, Janelle M. Spinazzola, T. F. Gallagher, Joan M. LaRovere, Diane E Balderson, Lauren Black, Keith A. Sutton, Richard Horgan, Monkol Lek, Terence R. Flotte

- Archive id: doi:10.1056/nejmoa2307798
- Published: 2023-09-27
- Venue: New England Journal of Medicine
- DOI: https://doi.org/10.1056/nejmoa2307798
- PMID: 37754285
- Citations: 318
- Source URL: https://doi.org/10.1056/nejmoa2307798
- PDF: https://pmc.ncbi.nlm.nih.gov/articles/PMC11288170/pdf/nihms-1998854.pdf
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [Gene & Cell Therapy](https://space-kitty.com/topics/gene-cell-therapy)

Cited in dossiers:
- [Gene & Cell Therapy: State of the Field (October 2026)](https://space-kitty.com/dossiers/gene-cell-therapy)

---
Space Kitty Archive · https://space-kitty.com · API: https://space-kitty.com/api/v1 · MCP: https://space-kitty.com/mcp · Premium: $0.20/request via x402 (Base Sepolia (testnet)). Metadata: arXiv (CC0), OpenAlex (CC0), Europe PMC (CC BY/CC0 works), ClinicalTrials.gov.