# CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy

Article · Marco A. Passini, Jie Bu, Eric M. Roskelley, Amy M. Richards, S. Pablo Sardi, Catherine R. O’Riordan, Katherine Wood Klinger, Lamya S. Shihabuddin, Seng H. Cheng

- Archive id: doi:10.1172/jci41615
- Published: 2010-03-16
- Venue: Journal of Clinical Investigation
- DOI: https://doi.org/10.1172/jci41615
- PMID: 20234094
- Citations: 292
- Source URL: https://doi.org/10.1172/jci41615
- Provenance: openalex

_Abstract not reproduced: its license does not permit redistribution. See the source URL._

Topics: [Gene & Cell Therapy](https://space-kitty.com/topics/gene-cell-therapy)

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