Treatment of retinitis pigmentosa due to MERTK mutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial
Nicola G. Ghazi, Emad B. Abboud, Sawsan R. Nowilaty, Hisham Alkuraya, Abdulrahman Alhommadi, Huimin Cai, Rui Hou, Wen‐Tao Deng, Sanford L. Boye, Abdulrahman M. Almaghamsi, Fahad Al Saikhan, Hassan A. Al-Dhibi, David G. Birch, Christopher Chung, Dilek Çolak, Matthew M. LaVail, Douglas Vollrath, Kirsten E. Erger, Wen‐qiu Wang, Thomas J. Conlon, Kang Zhang, William W. Hauswirth, Fowzan Sami Alkuraya
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Record
- Archive ID
- doi:10.1007/s00439-016-1637-y
- Published
- Jan 29, 2016
- Venue
- Human Genetics
- DOI
- 10.1007/s00439-016-1637-y
- PubMed
- 26825853
- Categories
- Retinal Development and Disorders
- Provenance
- openalex