Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia
Ding An, Jessica L. Schneller, Andrea Frassetto, Shi Liang, Xuling Zhu, Ji-Sun Park, Matt Theisen, Sue‐Jean Hong, Jenny Zhou, Raj Rajendran, Becca Levy, Rebecca Dean Howell, Gilles Besin, Vladimir Presnyak, Staci Sabnis, Kerry E. Murphy-Benenato, E. Sathyajith Kumarasinghe, Timothy Salerno, Cosmin Mihai, Christine Lukacs, Randy J. Chandler, Lin T. Guey, Charles P. Venditti, Paolo G.V. Martini
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Record
- Archive ID
- doi:10.1016/j.celrep.2017.11.081
- Published
- Dec 1, 2017
- Venue
- Cell Reports
- DOI
- 10.1016/j.celrep.2017.11.081
- PubMed
- 29262333
- Categories
- RNA Interference and Gene Delivery
- License
- cc-by-nc-nd
- Provenance
- openalex