Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector
Dawn E. Bowles, Scott McPhee, Chengwen Li, Steven James Gray, Jade Samulski, Angelique S. Camp, Juan Li, Bing Wang, Paul Edward Monahan, Joseph E. Rabinowitz, Joshua C. Grieger, Lakshmanan Govindasamy A, Mavis Agbandje‐McKenna, Xiao Xiao, Richard Jude Samulski
The abstract is not reproduced here because its license does not permit redistribution. Read it at the original source.
Record
- Archive ID
- doi:10.1038/mt.2011.237
- Published
- Nov 8, 2011
- Venue
- Molecular Therapy
- DOI
- 10.1038/mt.2011.237
- PubMed
- 22068425
- Categories
- Virus-based gene therapy research
- License
- cc-by-nc-nd
- Provenance
- openalex