A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice
Yang Yang, Lili Wang, Peter L. Bell, Deirdre McMenamin, Zhenning He, John White, Hongwei Yu, Chenyu Xu, Hiroki Morizono, Kiran Musunuru, Mark L. Batshaw, James M. Wilson
The abstract is not reproduced here because its license does not permit redistribution. Read it at the original source.
Record
- Archive ID
- doi:10.1038/nbt.3469
- Published
- Feb 1, 2016
- Venue
- Nature Biotechnology
- DOI
- 10.1038/nbt.3469
- PubMed
- 26829317
- Categories
- Virus-based gene therapy research
- Provenance
- openalex