A genome-editing strategy to treat β-hemoglobinopathies that recapitulates a mutation associated with a benign genetic condition

Elizabeth A. Traxler, Yu Yao, Yong‐Dong Wang, Kaitly J. Woodard, Ryo Kurita, Yukio Nakamura, Jim R. Hughes, Ross C. Hardison, Gerd A. Blobel, Chunliang Li, Mitchell J. Weiss

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Record

Archive ID
doi:10.1038/nm.4170
Published
Aug 15, 2016
Venue
Nature Medicine
DOI
10.1038/nm.4170
PubMed
27525524
Categories
Hemoglobinopathies and Related Disorders
Provenance
openalex

Topics