A long-term study of AAV gene therapy in dogs with hemophilia A identifies clonal expansions of transduced liver cells
Giang N. Nguyen, J.K. Everett, Samita Kafle, Aoife M. Roche, Hayley E. Raymond, Jacob S. Leiby, Christian M. Wood, Charles‐Antoine Assenmacher, Elizabeth P. Merricks, C Tyler Long, Haig H. Kazazian, Timothy C. Nichols, Frederic D. Bushman, Denise E. Sabatino
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Record
- Archive ID
- doi:10.1038/s41587-020-0741-7
- Published
- Nov 16, 2020
- Venue
- Nature Biotechnology
- DOI
- 10.1038/s41587-020-0741-7
- PubMed
- 33199875
- Categories
- Virus-based gene therapy research
- Provenance
- openalex