Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B
Amit Chunilal Nathwani, Edward G. D. Tuddenham, Savita Rangarajan, Cecilia Rosales, Jenny McIntosh, David C. Linch, Pratima Chowdary, Anne F. Riddell, Arnulfo Pie, Chris Harrington, James P. O’Beirne, Keith Smith, John Pasi, Bertil E. Glader, Pradip K. Rustagi, Catherine Y. Ng, Mark A. Kay, Junfang Zhou, Yunyu Spence, Christopher L. Morton, James A. Allay, John Coleman, Susan Sleep, John M. Cunningham, Deo Kumar Srivastava, and 7 more