CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia
Haydar Frangoul, David Altshuler, Maria Domenica Cappellini, Yi-Shan Chen, Jennifer Domm, Brenda K. Eustace, Juergen L. Foell, Josu de la Fuente, Stephan A. Grupp, Rupert Handgretinger, Tony W. Ho, Antonis Kattamis, Andrew M. Kernytsky, Julie A. Lekstrom-Himes, Amanda M. Li, Franco Locatelli, Markus Y. Mapara, Mariane de Montalembert, Damiano Rondelli, Akshay Sharma, Sujit Sheth, Sandeep Soni, Martin H. Steinberg, Donna Ann Wall, Angela Yen, and 1 more
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Record
- Archive ID
- doi:10.1056/nejmoa2031054
- Published
- Dec 5, 2020
- Venue
- New England Journal of Medicine
- DOI
- 10.1056/nejmoa2031054
- PubMed
- 33283989
- Categories
- Hemoglobinopathies and Related Disorders
- Provenance
- openalex