Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne’s Muscular Dystrophy

Angela Lek, Brenda L. Y. Wong, Allison M. Keeler, Meghan Blackwood, Kaiyue Ma, Shushu Huang, Katelyn Sylvia, Ana Rita Batista, Rebecca Artinian, Danielle Kokoski, Shestruma Parajuli, Juan Putra, Chrystalle Katte Carreon, Hart G.W. Lidov, Keryn G. Woodman, Sander Pajusalu, Janelle M. Spinazzola, T. F. Gallagher, Joan M. LaRovere, Diane E Balderson, Lauren Black, Keith A. Sutton, Richard Horgan, Monkol Lek, Terence R. Flotte

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Record

Archive ID
doi:10.1056/nejmoa2307798
Published
Sep 27, 2023
Venue
New England Journal of Medicine
DOI
10.1056/nejmoa2307798
PubMed
37754285
Categories
Virus-based gene therapy research
Provenance
openalex

Topics