Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne’s Muscular Dystrophy
Angela Lek, Brenda L. Y. Wong, Allison M. Keeler, Meghan Blackwood, Kaiyue Ma, Shushu Huang, Katelyn Sylvia, Ana Rita Batista, Rebecca Artinian, Danielle Kokoski, Shestruma Parajuli, Juan Putra, Chrystalle Katte Carreon, Hart G.W. Lidov, Keryn G. Woodman, Sander Pajusalu, Janelle M. Spinazzola, T. F. Gallagher, Joan M. LaRovere, Diane E Balderson, Lauren Black, Keith A. Sutton, Richard Horgan, Monkol Lek, Terence R. Flotte
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Record
- Archive ID
- doi:10.1056/nejmoa2307798
- Published
- Sep 27, 2023
- Venue
- New England Journal of Medicine
- DOI
- 10.1056/nejmoa2307798
- PubMed
- 37754285
- Categories
- Virus-based gene therapy research
- Provenance
- openalex