Efficacy and Safety of an Investigational Single-Course CRISPR Base-Editing Therapy Targeting PCSK9 in Nonhuman Primate and Mouse Models
Richard G. Lee, Anne Marie Mazzola, Maurine C. Braun, Colin Platt, Scott B. Vafai, Sekar Kathiresan, Ellen Rohde, Andrew M. Bellinger, Amit V. Khera
The abstract is not reproduced here because its license does not permit redistribution. Read it at the original source.
Record
- Archive ID
- doi:10.1161/circulationaha.122.062132
- Published
- Oct 31, 2022
- Venue
- Circulation
- DOI
- 10.1161/circulationaha.122.062132
- PubMed
- 36314243
- Categories
- CRISPR and Genetic Engineering
- Provenance
- openalex