CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy
Marco A. Passini, Jie Bu, Eric M. Roskelley, Amy M. Richards, S. Pablo Sardi, Catherine R. O’Riordan, Katherine Wood Klinger, Lamya S. Shihabuddin, Seng H. Cheng
The abstract is not reproduced here because its license does not permit redistribution. Read it at the original source.
Record
- Archive ID
- doi:10.1172/jci41615
- Published
- Mar 16, 2010
- Venue
- Journal of Clinical Investigation
- DOI
- 10.1172/jci41615
- PubMed
- 20234094
- Categories
- Neurogenetic and Muscular Disorders Research
- Provenance
- openalex