A Phase 2 Safety and Efficacy Study Evaluating CS-101 in Participants With β-Thalassemia Major

CorrectSequence Therapeutics Co., Ltd

View at source ↗Clinical trial
Source: ClinicalTrials.gov (U.S. National Library of Medicine), data processed 2026-10-29T09:00:05; modifications: selected fields only; whitespace normalized; brief summary truncated to 2,000 characters. Not a U.S. Government endorsement.

Brief summary

The goal of this open label, single-arm clinical study is to learn about the safety and efficacy of CS-101 in treating patients with β-Thalassemia Major

Source: ClinicalTrials.gov (U.S. National Library of Medicine), data processed 2026-10-29T09:00:05; modifications: selected fields only; whitespace normalized; brief summary truncated to 2,000 characters. Not a U.S. Government endorsement.

Trial details

status
NOT_YET_RECRUITING
phase
PHASE2
study type
INTERVENTIONAL
enrollment
20
sponsor
CorrectSequence Therapeutics Co., Ltd
conditions
β-thalassemia Major
interventions
GENETIC: CS-101 injection
start date
2026-04-05
start date type
ESTIMATED
primary completion date
2028-01-31
has results
false
data source
ClinicalTrials.gov
data processed
2026-10-29T09:00:05
modifications
selected fields only; whitespace normalized; brief summary truncated to 2,000 characters

Record

Archive ID
nct:NCT07489196
Published
Mar 24, 2026
Venue
ClinicalTrials.gov
ClinicalTrials.gov
NCT07489196
Categories
β-thalassemia Major
License
ClinicalTrials.gov terms (attribution, processing date, modifications noted)
Provenance
clinicaltrials

Topics